• A Cornucopia of Maximum Likelihood Algorithms

    Item Type Journal Article
    Author Kenneth Lange
    Author Xun-Jian Li
    Author Hua Zhou
    Date 2025-08-04
    Language en
    Library Catalog DOI.org (Crossref)
    URL https://www.tandfonline.com/doi/full/10.1080/00031305.2025.2526535
    Accessed 8/10/2025, 4:22:59 PM
    Pages 1-11
    Publication The American Statistician
    DOI 10.1080/00031305.2025.2526535
    Journal Abbr The American Statistician
    ISSN 0003-1305, 1537-2731
    Date Added 8/10/2025, 4:22:59 PM
    Modified 8/10/2025, 4:23:46 PM

    Tags:

    • mle
    • computing
    • maximum-likelihood-estimation
    • optimization
  • Bayesian Expectile Joint Model With Varying Coefficient for Longitudinal and Semi‐Competing Risks Data

    Item Type Journal Article
    Author Feng Gu
    Author Jiaqing Chen
    Author Jinjing Wang
    Author Yibo Long
    Author Xiaofan Wang
    Author Yangxin Huang
    Abstract ABSTRACT In the realm of clinical medical research, semi‐competing risks data are usually observed in practice, yet there are few studies on the joint models of longitudinal and semi‐competing risks data. In this paper, a joint model for longitudinal and semi‐competing risks data is proposed. Based on the expectile regression, a linear mixed‐effects longitudinal sub‐model is formulated, and a Cox proportional hazards survival sub‐model is considered under the framework of semi‐competing risks. The two sub‐models are linked by a shared longitudinal trajectory function. To accommodate the time‐varying relationship between the longitudinal response variable and covariates, as well as to introduce flexibility to the structural linkage between longitudinal and survival processes, we incorporate the time‐varying coefficients into the joint model in the form of nonparametric functions. The simultaneous Bayesian inference method is utilized to estimate the model parameters, which not only overcomes the convergence problem, but also improves the accuracy of the parameter estimation while effectively reducing the computational burden. The simulation studies are conducted to assess the performance of the proposed joint model and methodology. Finally, we analyze a dataset from the Multicenter AIDS Cohort Study to illustrate the real application of the proposed model and method. In both simulation studies and empirical analyses, joint modeling methods demonstrate performance that meets expected effects.
    Date 08/2025
    Language en
    Library Catalog DOI.org (Crossref)
    URL https://onlinelibrary.wiley.com/doi/10.1002/sim.70219
    Accessed 8/10/2025, 4:35:09 PM
    Volume 44
    Pages e70219
    Publication Statistics in Medicine
    DOI 10.1002/sim.70219
    Issue 18-19
    Journal Abbr Statistics in Medicine
    ISSN 0277-6715, 1097-0258
    Date Added 8/10/2025, 4:35:09 PM
    Modified 8/10/2025, 4:36:21 PM

    Tags:

    • rct
    • multiple-endpoints
    • competing-risk
    • bayes
    • cox-model
    • shared-parameter
    • expectile
  • Combining Missing Data Imputation and Internal Validation in Clinical Risk Prediction Models

    Item Type Journal Article
    Author Junhui Mi
    Author Rahul D. Tendulkar
    Author Sarah M. C. Sittenfeld
    Author Sujata Patil
    Author Emily C. Zabor
    Abstract ABSTRACT Methods to handle missing data have been extensively explored in the context of estimation and descriptive studies, with multiple imputation being the most widely used method in clinical research. However, in the context of clinical risk prediction models, where the goal is often to achieve high prediction accuracy and to make predictions for future patients, there are different considerations regarding the handling of missing covariate data. As a result, deterministic imputation is better suited to the setting of clinical risk prediction models, since the outcome is not included in the imputation model and the imputation method can be easily applied to future patients. In this paper, we provide a tutorial demonstrating how to conduct bootstrapping followed by deterministic imputation of missing covariate data to construct and internally validate the performance of a clinical risk prediction model in the presence of missing data. Simulation study results are provided to help guide when imputation may be appropriate in real‐world applications.
    Date 08/2025
    Language en
    Library Catalog DOI.org (Crossref)
    URL https://onlinelibrary.wiley.com/doi/10.1002/sim.70203
    Accessed 8/10/2025, 4:31:30 PM
    Volume 44
    Pages e70203
    Publication Statistics in Medicine
    DOI 10.1002/sim.70203
    Issue 18-19
    Journal Abbr Statistics in Medicine
    ISSN 0277-6715, 1097-0258
    Date Added 8/10/2025, 4:31:30 PM
    Modified 8/10/2025, 4:32:40 PM

    Tags:

    • bootstrap
    • validation
    • multiple-imputation
    • missing
  • Combining multiple imputation with internal model validation in clinical prediction modeling: a systematic methodological review

    Item Type Journal Article
    Author Sinclair Awounvo
    Author Meinhard Kieser
    Author Manuel Feißt
    Date 8/2025
    Language en
    Short Title Combining multiple imputation with internal model validation in clinical prediction modeling
    Library Catalog DOI.org (Crossref)
    URL https://linkinghub.elsevier.com/retrieve/pii/S0895435625002495
    Accessed 8/10/2025, 4:51:27 PM
    Pages 111916
    Publication Journal of Clinical Epidemiology
    DOI 10.1016/j.jclinepi.2025.111916
    Journal Abbr Journal of Clinical Epidemiology
    ISSN 08954356
    Date Added 8/10/2025, 4:51:27 PM
    Modified 8/10/2025, 4:52:00 PM

    Tags:

    • validation
    • multiple-imputation
    • review
    • missing
  • LASSO-Based Survival Prediction Modeling with Multiply Imputed Data: A Case Study in Tuberculosis Mortality Prediction

    Item Type Journal Article
    Author Md. Belal Hossain
    Author Mohsen Sadatsafavi
    Author James C. Johnston
    Author Hubert Wong
    Author Victoria J. Cook
    Author Mohammad Ehsanul Karim
    Date 2025-08-04
    Language en
    Short Title LASSO-Based Survival Prediction Modeling with Multiply Imputed Data
    Library Catalog DOI.org (Crossref)
    URL https://www.tandfonline.com/doi/full/10.1080/00031305.2025.2526545
    Accessed 8/10/2025, 4:29:44 PM
    Pages 1-12
    Publication The American Statistician
    DOI 10.1080/00031305.2025.2526545
    Journal Abbr The American Statistician
    ISSN 0003-1305, 1537-2731
    Date Added 8/10/2025, 4:29:44 PM
    Modified 8/10/2025, 4:30:16 PM

    Tags:

    • cox-model
    • multiple-imputation
    • lasso
    • missing
    • stacking
  • Nonparametric Assessment of Variable Selection and Ranking Algorithms

    Item Type Journal Article
    Author Zhou Tang
    Author Ted Westling
    Date 2025-10-13
    Language en
    Library Catalog DOI.org (Crossref)
    URL https://www.tandfonline.com/doi/full/10.1080/10618600.2025.2547064
    Accessed 10/15/2025, 11:24:15 AM
    Pages 1-12
    Publication Journal of Computational and Graphical Statistics
    DOI 10.1080/10618600.2025.2547064
    Journal Abbr Journal of Computational and Graphical Statistics
    ISSN 1061-8600, 1537-2715
    Date Added 10/15/2025, 11:24:15 AM
    Modified 10/15/2025, 11:25:24 AM

    Tags:

    • variable-importance
    • ranking-selection
  • Novel Clinical Trial Design With Stratum‐Specific Endpoints and Global Test Methods for Rare Diseases With Heterogeneous Clinical Manifestations

    Item Type Journal Article
    Author Emily Shives
    Author Yared Gurmu
    Author Wonyul Lee
    Author Emily Morris
    Author Yan Wang
    Abstract ABSTRACT Many rare disease clinical trials are underpowered to detect a moderate treatment effect of an investigational product due to the limited number of participants available for the trials. In addition, given the complex, multisystemic nature of many rare diseases, it is challenging to confidently prespecify a single primary efficacy endpoint that is applicable to all trial participants with a heterogeneous clinical manifestation of their disease. Traditional trial designs and analysis methods often used in more common diseases to analyze the same endpoint(s) for all patients may be inefficient or impractical for a rare disease with heterogeneous clinical manifestations. To address these issues, we propose a novel trial design and analytic approach that allows for an evaluation of stratum‐specific efficacy endpoints in a broader population of participants. We develop several nonparametric global test methods that can accommodate the novel design and provide global evaluation of treatment effects. Using a case example in patients with Fabry disease, our simulation studies illustrate that the novel design evaluated using the global test methods may be more sensitive to detect a treatment effect compared to the traditional design that uses the same endpoint(s) for all patients.
    Date 08/2025
    Language en
    Library Catalog DOI.org (Crossref)
    URL https://onlinelibrary.wiley.com/doi/10.1002/sim.70206
    Accessed 8/10/2025, 4:37:45 PM
    Volume 44
    Pages e70206
    Publication Statistics in Medicine
    DOI 10.1002/sim.70206
    Issue 18-19
    Journal Abbr Statistics in Medicine
    ISSN 0277-6715, 1097-0258
    Date Added 8/10/2025, 4:37:45 PM
    Modified 8/10/2025, 4:38:13 PM

    Tags:

    • multiple-endpoints
    • global-test
    • rare-disease
  • Second-generation p-values: Improved rigor, reproducibility, & transparency in statistical analyses

    Item Type Journal Article
    Author Jeffrey D. Blume
    Author Lucy D’Agostino McGowan
    Author William D. Dupont
    Author Robert A. Greevy
    Editor Neil R. Smalheiser
    Date 2018-3-22
    Language en
    Short Title Second-generation p-values
    Library Catalog DOI.org (Crossref)
    URL https://dx.plos.org/10.1371/journal.pone.0188299
    Accessed 9/4/2025, 8:51:13 AM
    Volume 13
    Pages e0188299
    Publication PLOS ONE
    DOI 10.1371/journal.pone.0188299
    Issue 3
    Journal Abbr PLoS ONE
    ISSN 1932-6203
    Date Added 9/4/2025, 8:51:13 AM
    Modified 9/4/2025, 8:51:41 AM

    Tags:

    • multiplicity
    • confidence-intervals
    • inference